The Muscular Dystrophy Association (MDA) and Coalition to Cure Calpain 3 (C3) announced today collaborative funding of a $300,000 research grant to ...
Patidistrogene bexoparvovec is a gene therapy commercialized by Sarepta Therapeutics, with a leading Phase II program in Limb-Girdle Muscular Dystrophy.
Ribitol (BBP-418) is under development for the treatment of limb-girdle muscular dystrophy type 2I/R9 (LGMD2I/R9). It acts by restoring glycosylate alpha- dystroglycan (aDG) substrate. It is an oral ...
His coaches sent him to get checked out. Gabriel Vergara, who lives with muscular dystrophy, shown outside his apartment in Hialeah. MATIAS J. OCNER [email protected] After a blur of tests ...