An approval would make RGX-121 the first gene therapy for Hunter syndrome, which is progressive and causes a range of ...

Denali Therapeutics Inc.'s stock remains stable despite trial setback in ALS. BLA filing for MPS II treatment on track. Click ...

Hunter syndrome affects over 2,000 individuals ... The condition is characterized by a deficiency of the iduronate-2-sulfatase (IDS) enzyme, leading to a range of symptoms, including organ dysfunction ...

Denali Therapeutics Inc. (NASDAQ: DNLI), today announced that the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy Designation for tividenofusp alfa (DNL310) for the treatment ...

A viral outbreak in China sounds alarmingly familiar to 2019, back in the days before most of us had ever heard of the “severe acute respiratory syndrome coronavirus 2”, better known as Covid-19.

Kidney failure symptoms may begin so gradually that you don't really notice swelling, joint pain, or changes in how you urinate (pee). Or, you may think that itchy skin and other signs are due to ...

If you buy something, we may earn an affiliate commission. If there’s one thing you don’t want to endure, it’s the symptoms of norovirus, a brutal stomach bug that tends to cause relentless ...

Storyline: When his abusive father’s actions cause him to escape home, Kraven finds haven in a sanctuary and turns into a hunter only to know that he’s being hunted As a fan of Hollywood films ...

The controversial medical diagnosis of shaken baby syndrome can send parents to jail. What if the symptoms are caused by something else? Nick Flannery with his older son. Suspicions of abusive ...