CRISPR gene editing based treatment reduced HAE attacks rates by up to 80%. NTLA-2002 was well tolerated by patients. The ...

Researchers have used whole-genome CRISPR interference screening to identify the “Achilles Heel” of drug-resistant ...

Gliocidin selectively kills glioblastoma cells by inhibiting nucleotide synthesis, showing potential as a therapeutic option ...

OHSU one of 20 sites hosting the clinical trial for the amyloidosis therapy. Masri, who is overseeing the trial in Oregon, told The Lund Report that finding a way to deliver gene therapy directly to ...

By targeting the TTR gene directly in the liver, the therapy “has opened up the door” to permanent treatment, says Sarah ...

A breakthrough tool called Helicase-Assisted Continuous Editing (HACE) allows scientists to create precise genetic mutations ...

A CRISPR-Cas9-based investigational therapy was linked with a drop in serum transthyretin (TTR) levels in patients with ...

A recent study unveiled a key enzyme involved in producing selenoproteins, opening new strategies for treating certain types of cancer in children.

However, instead of using the Cas9 enzyme that is often used to edit DNA molecules, the investigators relied on a different ...

A recent study from the University of Würzburg unveiled a key enzyme involved in producing selenoproteins, opening new ...

Harvard researchers pioneered a method called HACE for targeted gene mutations, advancing genetic research potential.

CRISPR-Cas9 is a powerful gene-editing tool that allows scientists to modify DNA in living organisms precisely. It works like ...