Somatic gene transfer with vectors such as adeno-associated virus (AAV) can overcome these limitations. ReGenX's AAV Vector Technology gives extremely efficient and stable gene expression in ...

DOI: 10.1056/NEJMoa2410597 Johnny Mahlangu, Could Lentivirus Overcome the AAV Gene-Therapy Challenges in Hemophilia A?, New England Journal of Medicine (2024). DOI: 10.1056/NEJMe2414214 ...

Researchers are making strides in improving gene therapies for genetic diseases, particularly chronic kidney disease, using adeno-associated virus, or AAV, vectors. While AAV-based treatments have ...

Correctly measuring AAV vectors, as they are called, is critical to their safety and efficacy. In a recently released study, researchers at the National Institute of Standards and Technology ...