Somatic gene transfer with vectors such as adeno-associated virus (AAV) can overcome these limitations. ReGenX's AAV Vector Technology gives extremely efficient and stable gene expression in ...

Researchers are making strides in improving gene therapies for genetic diseases, particularly chronic kidney disease, using adeno-associated virus, or AAV, vectors. While AAV-based treatments have ...

DOI: 10.1056/NEJMoa2410597 Johnny Mahlangu, Could Lentivirus Overcome the AAV Gene-Therapy Challenges in Hemophilia A?, New England Journal of Medicine (2024). DOI: 10.1056/NEJMe2414214 ...

1 department of Rheumatology and Immunology, Peking University International Hospital 2 department of Rheumatology and Immunology, The First affiliated hospital of Chinese PLA general Hospital, ...

Correctly measuring AAV vectors, as they are called, is critical to their safety and efficacy. In a recently released study, researchers at the National Institute of Standards and Technology ...