Rare eye diseases are the leading cause of untreatable blindness in Europe and affect people of all ages. The RESTORE VISION ...

President Donald Trump’s nominee for FDA Commissioner, Martin A. Makary, MD, sought to assure senators that if confirmed, he would support efforts to expedite reviews of new drugs indicted for rare ...

With a U.S. green light for its encapsulated cell therapy technology in the bag, privately held biotech Neurotech ...

March 7, 2025 – The FDA has approved a new gene therapy for macular telangiectasia type 2 (MacTel), a rare eye disease that causes vision loss. The approval marks the first and only ...

Prince Frederik of Luxembourg died from a genetic disease called PolG, but experts hope his passing could bring more ...

Board members Dr. Laura Landerman Garber and Nancy Biederman update the work of NH's council, legislation and an upcoming ...

Like in many rare diseases, there are some dire statistics ... the best possible start when developing treatments for eye diseases, The Foundation Fighting Blindness has founded the My Retina ...

Alnylam has said it will not proceed with a clinical trial of its RNAi drug vutrisiran in the rare eye disorder Stargardt disease – at least for now – tying its decision to President Joe Biden ...