Denali Therapeutics Neurodegenerative Disease Platform Sparks Analyst Optimistic
William Blair has initiated coverage on Denali Therapeutics Inc (NASDAQ:DNLI), a company focused on developing drugs for ...
WebMD1mon
Hunter Syndrome (MPS II)
What Is Hunter Syndrome (MPS II)? Hunter syndrome, also called mucopolysaccharidosis II or MPS II, is a rare disease that's passed on in families. It mainly affects boys. Their bodies can't break ...
Hosted on MSN11mon
Fetal therapy offers hope for unborn patients suffering from the rare genetic disease Hunter Syndrome
Before Ryann was born, a prenatal screening revealed he had a genetic disorder known as Hunter Syndrome or Mucopolysaccharidosis Type II. It is a rare genetic disorder that Queen's little brother ...
pharmaphorum7y
Shire's Hunter Syndrome cognitive impairment drug fails
Shire’s attempts to develop a drug for cognitive impairment from the rare inherited disease Hunter Syndrome has failed to produce results. The company’s Elaprase (idursulfase) is already ...
University of Manchester2mon
Groundbreaking gene therapy trial for Hunter syndrome opens
The UK regulatory authorities have approved the first ever trial of a revolutionary gene therapy for young children diagnosed with Hunter syndrome, a devastating rare lysosomal storage disorder. Five ...
University of Manchester4y
University announces partnership with AVROBIO for Hunter syndrome gene therapy
The University of Manchester has announced today a groundbreaking gene therapy partnership to ease the lifelong suffering of people with Hunter syndrome. The University has agreed to a worldwide ...
조선일보24d
GC Green Cross secures Russian approval for Hunterase ICV, treatment for Hunter syndrome
GC Green Cross announced on the 11th that its severe Hunter syndrome treatment ‘Hunterase ICV’ has received product approval from the Russian Federal Ministry of Health. This is the first ...