Since two gene therapies were approved for sickle cell disease in late 2023, only a handful of patients have started the ...
But for a brief moment on a recent December morning, Wedam, 19, who has sickle cell disease, allowed himself to believe what his doctors had been ... D.C., for his stem cell collection — the first ...
Texas Children's Hospital and Baylor College of Medicine are providing medication and other aid to fight sickle cell disease ...
HHS challenges Vertex Pharmaceuticals' fertility services program, alleging violations of anti-kickback laws linked to its ...
YolTech Therapeutics, a clinical-stage gene editing company dedicated to delivering lifelong cures, announced the initiation of a clinical trial for YOLT-204, an investigational therapy for the ...
For columnist Mary Shaniqua, one of the hardest aspects of sickle cell is its unpredictability, such as the sudden onset of a ...
The US biotech said the suspected serious adverse reaction reported in the phase 1/2 study of LentiGlobin gene therapy for sickle cell disease was unlikely to be related to the virus vector used ...