In a finding with implications for one of the most promising cutting-edge medical treatments, researchers evaluated several measurement techniques commonly used in gene therapy.

Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and accurate ...

Germline gene therapy and somatic gene therapy are two quite different proposals, and the legitimate concerns and risks of the former should not be used to stall progress on the latter. The ...

Gene therapy has been available since 2022 for hemophilia B and since 2023 for hemophilia A, yet some major medical institutions have barely treated any patients so far. What’s the holdup?

However, CRISPR brings an important advantage over these other techniques: it is much easier and faster to use ... VERVE-101 works by permanently inactivating the PCSK9 gene, which plays a key role in ...

As gene therapy techniques become more refined and successful, they offer the possibility of not just managing hemophilia but potentially curing it, eliminating the lifelong need for clotting ...

Techniques that cause multipotent adult mesenchymal ... endogenous regenerative activities in the OA joint. Targeted gene therapy might further enhance these activities of MSCs.