Despite intensified research endeavors in CVD, the diagnosis, management, and treatment of these conditions ... Screening and Validation Methods for Alternative Splicing Events AS plays crucial roles ...

offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root cause of a disease at the genetic level, this cutting-edge ...

Alternative splicing (AS), a critical process for gene expression regulation ... can contribute to the development of cardiovascular diseases. In addition, multiple hereditary heart-related ...

Late-onset Alzheimer's disease is a debilitating ... we can potentially use it to treat both populations," Ma said. By expanding our understanding of genetic risk factors beyond APOE ε4, this ...

Stargardt disease also known as Stargardt macular degeneration, is commonly caused by changes in a gene, ABCA4. This gene influences how your body uses Vitamin A. There is currently no cure ...

There's new hope for couples who have discovered a genetic disease that may affect their future children. Doctors in the UAE are pioneering new methods that will allow them to treat a genetic ...

The scientific advancements of the past 30 years have transformed our understanding of the potential of gene ... with rare diseases still do not have access to the right care or treatment.

The Muscular Dystrophy Association celebrates the FDA approval of Evrysdi in tablet form, a more accessible treatment option ...

Cure Rare Disease (CRD) is a nonprofit biotechnology company focused on developing genetic medicines for rare and ultra-rare diseases. CRD is committed to accelerating the development of ...