“There are more than 100,000 adults with DM1 in the US and Europe, making it the most common adult-onset muscular dystrophy. We believe that the market opportunity for a new DM1 therapy is very ...
Ryan Getzlaf and Hawken Miller help to inspire each other every day, and Miller’s battle with Duchenne muscular dystrophy has given Getzlaf a cause to champion away from the rink. Take a look at ...
have been diagnosed with Duchenne Muscular Dystrophy, a rare progressive muscle loss disease. On Saturday at Cherry Rock Park, the group held a Zippy Mile to raise funds to help fight the disease ...
At the Breakthroughs in Muscular Dystrophy special meeting held in Chicago Nov. 19-20, 2024, and organized by the American Society of Gene & Cell Therapy (ASGCT), multiple interventions at the RNA ...
Regenxbio reported Monday the first clinical evidence showing improved muscle function in boys with Duchenne muscular dystrophy following treatment with its experimental gene therapy. The positive ...