The biomedical research community should act quickly and decisively to divorce the two before pushing ahead with well-conceived postnatal and fetal somatic gene therapy protocols. That gene ...

might require prenatal or fetal gene therapy to minimize morbidity. Gene therapy is also being considered for the treatment of inflammatory and infectious diseases of the lung. In these cases ...

More information: Rebecca L Wilson et al, Placental gene therapy in nonhuman primates: a pilot study of maternal, placental, and fetal response to non-viral, polymeric nanoparticle delivery of ...

When asked to picture the ideal cure for sickle-cell disease, molecular biologist Stefano Rivella, a researcher at Children’s Hospital of Philadelphia (CHOP), Pennsylvania, didn’t gaze into ...

The first therapy that uses gene-editing is to be offered on the NHS ... When we are still in the womb, our bodies use "fetal haemoglobin" to pull oxygen out of our mother's bloodstream.

Formerly the 2022 American Society for Gene and Cell Therapy Career Development Award and an NSF Postdoctoral Research Fellowship in Biology. Environmental Health: Investigating the Impact of Micro- ...

Treatments for rare diseases are hard to create and expensive to deliver, but there is new hope for editing the software of ...

The HCM heart demonstrates fetal gene reprogramming and inhibition of SP1 or EGR1 can alleviate the development of HCM in mice. Hypertrophic cardiomyopathy (HCM), the most common inherited heart ...

Orna Therapeutics and Vertex will use lipid nanoparticle system to develop gene-editing therapies for people with SCD and TDT ...

Gene therapy is referred to as a medical technique ... Rapid engraftment and high levels of fetal hemoglobin (HbF) in treated patients were observed, potentially outperforming other gene therapies ...

The Gates Foundation will invest up to $50 million to support Tessera's SCD gene editing treatment, the company said.