Last week, the company started rolling submissions for a biologics license application (BLA) for deramiocel as a treatment for DMD cardiomyopathy with the US Food and Drug Adminis ...
trial for its Duchenne muscular dystrophy (DMD) cell therapy, deramiocel. Last week, the company started rolling submissions for a biologics license application (BLA) for deramiocel as a treatment ...
It is a type of gene therapy that aims to restore the production of dystrophin protein in the muscles, which can help slow down or stop the progression of DMD. WVE-N531 has shown strong results in ...