With Brineura, indicated for the treatment of children with Batten disease (or CLN2 disease), this discrepancy was a contributing factor. Although CLN2 disease is an ultra-rare disease based on ...

Also known as Batten disease, CLN2 is a progressive condition caused by the deficiency of the enzyme tripeptidyl peptidase 1. This results in the abnormal storage of proteins and lipids in neurons ...

Mar. 5, 2025 — Research shows that a common type of diabetes medication could help cancer patients make a better long-term recovery. Many cancer patients go on to develop heart failure ...

After hours: March 6 at 5:22:11 PM EST Loading Chart for LXEO ...

June 10, 2024 — Scientists have grown 'mini-guts' in the lab to help understand Crohn's disease, showing that 'switches' that modify DNA in gut cells play an ... Major Cause of Inflammatory ...

Disease prevention is a procedure through which individuals, particularly those with risk factors for a disease, are treated in order to prevent a disease from occurring. Treatment normally begins ...