Cystic fibrosis (CF) is a life-threatening genetic disease affecting multiple organ systems, with pancreatic dysfunction representing a critical and often overlooked complication.
Cystic fibrosis (CF) is a life-threatening genetic disease affecting multiple organ systems, with pancreatic dysfunction representing a critical and ...
Arcturus Therapeutics initiates patient dosing in phase 2 multiple ascending dose studies for CF and OTC deficiency: San Diego Wednesday, January 8, 2025, 13:00 Hrs [IST] Arcturus ...
Cystic fibrosis transmembrane conductance regulator (CFTR) modulators are a class of medications that help improve the function of the atypical protein causing cystic fibrosis. According to the ...
Like Vertex’s other CF therapies, Alyftrek is a modulator of the CFTR a protein that regulates the movement of chloride ions into and out of cells. Alyftrek’s approval is based on clinical ...