Subcomponent Scores in Children with Ataxia-Telangiectasia (A-T) describes the baseline ICARS subcomponent scores by age in a cross-sectional analysis of treatment-naive patients from the ATTeST ...

Dirk Thye, M.D., Quince’s Chief Executive Officer and Chief Medical Officer, said, "We are pleased to report accelerating ...

Key findings reported in the poster presentation, titled Treatment-Emergent Adverse Events (TEAEs) in Children With Ataxia-Telangiectasia Treated for One Year With Intra-Erythrocyte ... Dose Pediatric ...

The new PDUFA target date is March 18, 2025. The Food and Drug Administration (FDA) has extended the review period for the Biologics License Application (BLA) for NT-501 (revakinagene taroretcel ...

Oct. 30, 2024 — Chronic, low-level lead poisoning is a major risk factor for cardiovascular disease in adults and cognitive deficits in children, even at levels previously thought to be safe ...

Disease prevention is a procedure through which individuals, particularly those with risk factors for a disease, are treated in order to prevent a disease from occurring. Treatment normally begins ...