South African regulators decided Vertex Pharmaceuticals has provided sufficient access to its cystic fibrosis medications, ...

Krystal Biotech, Inc. KRYS announced initial clinical data updates on its two inhaled genetic medicine pipeline candidates, ...

According to estimates, more than 400 people in South Africa live with cystic fibrosis, with many requiring specialised and ...

Mean change in chloride transport from baseline to end of treatment low dose: −6.8 mV (p = 0.004) high dose: −3.4 mV (p = 0.025) combined groups: −5.4 mV (p < 0.001) CF = cystic fibrosis ...

The treatment is designed to address the underlying cause of cystic fibrosis by delivering a therapeutic gene that allows lung cells to make a working CFTR protein and prevention infection.

Results underscore the widespread challenges faced by individuals with cystic fibrosis in managing health care expenses.

The initiative, conducted in collaboration with Intellia Therapeutics, aims to develop new treatments for cystic fibrosis (CF), including for patients with genotypes that are non-responsive or ...

Judah was diagnosed with cystic fibrosis at 2 weeks old and with the help of Make-A-Wish, he was able to make his musical ...

Jefferies upgrades Vertex Pharmaceuticals to Buy, highlighting a promising pipeline and $5 billion-$7 billion growth ...

A stunning forest of over 60 Christmas trees has transformed Wellington Airport into a festive wonderland, all in support of ...

Professor Alan Smyth from Queen’s University has been awarded ‘Outstanding Clinical Researcher’ at the Cystic Fibrosis Trust ...