In someone who has SCD, the hemoglobin is abnormal, which causes the red blood cells to become hard and sticky and look like a C-shaped farm tool called a “sickle.” “The way I would explain ...
the gene editing tool that won its inventors the Nobel Prize in 2020. The other is made by Bluebird Bio and works differently. “Sickle cell disease is a rare, debilitating and life-threatening ...