Viral vectors introduce genes and gene editing sequences into cells, and are a popular platform for gene therapy due to their safety and efficacy features. Adeno-associated viral (AAV) vectors in ...

The integrated viral DNA is termed 'provirus ... capacity of hitherto used gretroviral vectors. They are already in use in current clinical gene therapy trials. Successful gene therapeutic ...

New research by Oregon Health & Science University scientists has uncovered multiple factors to improve gene delivery to the ...

Researchers have developed an innovative therapeutic platform by mimicking the intricate structures of viruses using ...

Deficiencies in the SLC6A1 gene, encoding the γ-aminobutyric acid transporter GAT-1, are associated with infantile encephalopathy with intellectual disability. Like other neurodevelopmental disorders, ...

Scientists have developed an innovative therapeutic platform by mimicking the intricate structures of viruses using artificial intelligence (AI).

When two halves of a large therapeutic gene are encoded into adeno-associated virus (AAV) vectors, which are the most commonly used vectors for gene therapy because they are safe and don't cause ...

GEMMA Biotherapeutics, founded by Jim Wilson earlier this year, will use the money to expand its operations and gene therapy ...

Integrated gene therapy successfully treated Haemophilia A in India, providing long-term relief without bleeding episodes for ...

The results were obtained with a single intramuscular administration of the therapeutic viral vectors ... the intramuscular administration of a gene therapy for the treatment of MASH, a liver ...

LUND, Sweden & EVRY, France--(BUSINESS WIRE)--Hansa Biopharma, “Hansa” (Nasdaq Stockholm: HNSA) and Genethon, a pioneer and a leader in gene therapy research and development for rare genetic ...