In recent years, a growing understanding of myotonic dystrophy type 1 (DM1)—an often fatal, devastating, rare neuromuscular disorder that causes muscle weakness and other life-limiting ...

in patients with myotonic dystrophy type 1 (DM1), also known as Steinert disease. The third clinical program is dubbed ARO-MMP7 and targets idiopathic pulmonary fibrosis, a chronic disease that ...

Patients with myotonic dystrophy have smaller hearts, and lower systolic and diastolic blood pressures and pulse rates. They have impaired autonomic reflexes, measured by orthostatic, Valsalva ...

AOC 1001 for myotonic dystrophy type 1 (DM1) – within the next few months. DM1 (formerly known as Steinert disease) is caused by a defect in the DMPK gene on chromosome 19 and is a form of ...