1). Like many other muscular dystrophies ... ARTHEx also has ATX-01 in preclinical testing for myotonic dystrophy type 2 (DM2). “Although DM2 is caused by a different mutation, it similarly ...

People with myotonic dystrophy type 1 (DM1), the most common adult-onset form of muscular dystrophy, progressively lose ...

People with Myotonic Dystrophy Type 1 (DM1), the most common adult-onset form of muscular dystrophy, progressively lose ...

In 2023, the analyst reported a breakdown of Myotonic Dystrophy Type 1 cases in the US, with nearly 540 congenital, 3,893 infantile, 1,515 juvenile, 39,686 adult-onset, and 8,435late-onset cases.

The analysis indicates that in 2023, the US had approximately 43,255 diagnosed cases of Myotonic Dystrophy Type 1 and 10,815 cases of Myotonic Dystrophy Type 2. This data highlights a significant ...

global Phase I/II ACHIEVE trial in adults with myotonic dystrophy type 1 (DM1). The ACHIEVE trial currently includes 56 participants and is fully enrolled through the 6.8 mg/kg Q8W cohort ...

Myotonic Dystrophy Type 1 (DM1) arises from an expanded microsatellite CTG repeat ... We have generated constructs composed of APEX2 fused to MBNL1/2, which localizes the APEX2 protein to the RNA foci ...

Forty-seven of the patients with myotonic dystrophy took part in full testing ... who did not know the patient's diagnosis. A paired 2-tailed Student's t-test was used to compare continuous ...

(MENAFN- GlobeNewsWire - Nasdaq) Dublin, Dec. 18, 2024 (GLOBE NEWSWIRE) -- The "Myotonic Dystrophy - Epidemiology Forecast - 2034" report has been added to ResearchAndMarkets.com's offering.