It is not surprising that most disease-modifying therapies in development ... restored muscle force and reduced electrophysiological myotonia. Target engagement was detected in tissues including ...

Twenty-year-old Giacomo Naylor, 16-year-old Lukas Naylor, 13-year-old Isadora Naylor and Gianna Naylor were all born with ...

Keep abreast with the latest news related to Myotonic Dystrophy there are 6 news items on Myotonic Dystrophy that covers updates, breakthroughs and in-depth reports. We provide you with a free ...

An increase in research and development (R&D) activities in myotonic dystrophy is expected to drive market growth by enhancing the understanding of the disease, accelerating drug discovery ...

Patients with myotonic dystrophy and either any indication or a family history of myotonic heart disease should have at least a yearly ECG (including at least the lead which consistently best ...

Ending the diagnostic journey for patients, particularly those with rare diseases, improves patients' quality of life while ...

In Japan, the 2023 data shows nearly 1,565 cases of Myotonic Dystrophy among children and 11,170 cases among adults. This distribution underscores the considerable prevalence in both age groups, ...

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced that Dr. Reshma Kewalramani, Chief Executive Officer and President, will present at the 43rd Annual J.P. Morgan Healthcare Conference ...

Myotonic Dystrophy Pipeline Report Introduction 2. Myotonic Dystrophy Pipeline Report Executive Summary 3. Myotonic Dystrophy ...