Bray has spinal muscular atrophy, a rare degenerative disease that's gradually robbed him of the ability to move his muscles. At age 29, he can no longer move his head, arms, hands or legs.
US FDA grants orphan drug designation to NMD Pharma’s NMD670 to treat patients with Charcot-Marie-tooth disease: Aarhus, Denmark Tuesday, January 7, 2025, 16:00 Hrs [IST] NMD Ph ...