Rising health awareness, increasing prevalence of various forms of mucopolysaccharidosis worldwide, continuous advances in ...
What Is Hunter Syndrome (MPS II)? Hunter syndrome, also called mucopolysaccharidosis II or MPS II, is a rare disease that's passed on in families. It mainly affects boys. Their bodies can't break ...
Politicians from both Houses of Parliament have gathered to mark the death of Queen Elizabeth II and share their memories ... special tributes in Parliament. MPs and ex-PMs paid their respects ...
DNL310, or tividenofusp alfa, is an Enzyme Transport Vehicle (ETV)- enabled iduronate-2-sulfatase (IDS) replacement therapy in development for MPS II (Hunter syndrome). In September, Denali ...
The company separately said it has started treating patients within a Phase III trial testing an ASO drug for Angelman syndrome.