How can you measure a person's quality of life? For columnist Patrick Moeschen, the key is deciding for yourself what a good ...

Dublin, Nov. 29, 2024 (GLOBE NEWSWIRE) -- The "Limb-Girdle Muscular Dystrophy (LGMD): Competitive Landscape" report has been added to ResearchAndMarkets.com's offering. This report provides a data ...

Sarepta Therapeutics has completed enrolment and dosing in the global Phase III EMERGENE trial of its investigational gene ...

ATA-200 is a one-time gene therapy for the treatment of γ-sarcoglycan related limb-girdle muscular dystrophy Type 2C/R5 (LGMD2C/R5), a serious and debilitating condition that affects children and ...

Muscular dystrophy is a group of diseases that make muscles weaker and less flexible over time. It is caused by a problem in the genes that control how the body keeps muscles healthy. For some ...

Research Grants and 7 Development Awards for Fellowship Trainees Will Fund Critical Research Across Multiple Neuromuscular ...

(AskBio), a gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, today announced that AB-1003 (also known as LION-101) has received rare pediatric disease ...

StitchR enabled expression of the protein Dysferlin, which is lacking in individuals with limb girdle muscular dystrophy type 2B/R2, as well as the protein Dystrophin, which is absent in patients ...

Tina Fegley, who has a form of Limb-girdle muscular dystrophy and uses a wheelchair, admits to PEOPLE that navigating the dating world hasn’t been easy. “I feel like most guys would see the ...

The Bill & Melinda Gates Foundation will invest up to $50 million in Tessera’s in vivo sickle cell therapy. Elsewhere, Cara ...

The Muscular Dystrophy Association (MDA) and Coalition to Cure Calpain 3 (C3) announced today collaborative funding of a $300,000 research grant to ...