FDA approves Kebilidi for aromatic L-amino acid decarboxylase deficiency
The U.S. Food and Drug Administration has approved PTC Therapeutics' Kebilidi (eladocagene exuparvovec-tneq) for the ...
L-Lysine is an essential amino acid. Here's why it matters.
L-Lysine, or lysine, is an amino acid - which are organic compounds that link together to form proteins. Lysine is considered ...
FierceBiotech8 小时
PTC sells priority review voucher from Kebilidi approval for $150M
PTC Therapeutics may reeling from the failure of its amyotrophic lateral sclerosis (ALS) drug utreloxastat yesterday, but the ...
EurekAlert!1 天
A study discovers how algae produce a hormone they use to communicate
"The auxin production pathway we demonstrated here is very simple and very common. It involves the L-amino acid oxidase (LAO1 ...
WebMD8 天
First Brain-Injected Gene Therapy Approved by FDA
The FDA has granted fast-track approval for a groundbreaking gene therapy indicated for a rare genetic disorder called ...
verywellhealth1 天
How Isoleucine Supports Exercise Recovery and Overall Health
Isoleucine is an essential amino acid classified as a branched-chain amino acid. Read on to learn about the potential uses ...
FDA Approves PTC's Kebilidi As First Gene Therapy To Treat AADC Deficiency
The U.S. Food and Drug Administration approved PTC Therapeutics, Inc.'s Kebilidi (eladocagene exuparvovec-tneq) gene therapy for the ...