The goal is to improve outcomes of children identified with, or at risk for, Krabbe Disease. To achieve this goal, the institute established in 2006 the NYS Krabbe Consortium, a multidisciplinary ...

Ibudilast is under clinical development by MediciNova and currently in Phase II for Coronavirus Disease 2019 (COVID-19) Associated Acute Respiratory Distress Syndrome.

GEMMA Biotherapeutics, the start-up that gene therapy pioneer Jim Wilson founded earlier this year, has raised $34 million in ...

Piracha, MDLipoid pneumonia (LP) is a rare, non-infectious condition that occurs when oil or fat (lipids) molecules enter the ...

Treatments can help manage condition, no known cure Diagnosed by medical professional Requires lab test or imaging Common for ages 5 and younger May be dangerous or life threatening The disease is ...

Jackson Garwood, from East Tilbury in Essex, was given a year to live at the age of one when he was diagnosed with Krabbe disease. His father Darren Garwood, 40, has written the fourth in a series ...