BioMarin’s Voxzogo has been shown to increase growth rates in children with hypochondroplasia, a genetic cause of very short stature, in a phase 2 trial. Hypochondroplasia is a form of skeletal ...
More information: Andrew Dauber et al, Vosoritide treatment for children with hypochondroplasia: a phase 2 trial, eClinicalMedicine (2024). DOI: 10.1016/j.eclinm.2024.102591 Provided by Children's ...