BioMarin’s Voxzogo has been shown to increase growth rates in children with hypochondroplasia, a genetic cause of very short stature, in a phase 2 trial. Hypochondroplasia is a form of skeletal ...

Hypochondroplasia specific height SDS increased by 0.38 SD, according to the trial published in eClinicalMedicine. The authors studied 24 children with hypochondroplasia.