Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and accurate ...

In a finding with implications for one of the most promising cutting-edge medical treatments, researchers evaluated several measurement techniques commonly used in gene therapy.

Common measurements for modified adeno-associated viruses (AAVs), a gene therapy delivery method, showed substantial ...

The CONNECT2-EDO51 phase 2 trial looks at PGN-EDO51, an investigational therapy for Duchenne muscular dystrophy (DMD), and is still ongoing in the United Kingdom. The most-read gene therapy ...

Researchers have developed a highly efficient gene editing therapy that could potentially ... the team demonstrated the effectiveness of their technique in multiple models, including human tissues ...

Researchers have developed a highly efficient gene editing therapy that could potentially treat Stargardt disease ... Importantly, the team demonstrated the effectiveness of their technique in ...

This research deepens our understanding of the evolutionary origin of DGRs and may be applicable to future gene-editing techniques. The findings are published in the journal Nature. More ...