Germline gene therapy and somatic gene therapy are two ... is often at the center of objections to the procedure. So far, only a few studies of this potential have been published, and none have ...
Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and accurate ...
Gene therapy has been available since 2022 for hemophilia B and since 2023 for hemophilia A, yet some major medical institutions have barely treated any patients so far. What’s the holdup?
And as one would expect or hope to see in a gene therapy trial, there was a significant and marked reduction in the use of factor.” Moving forward, he said, the message to clinicians is that ...