India is progressing in cell and gene therapy. Research includes treatments for leukemia, hemophilia-A, sickle-cell anemia, ...

who is now able to hear thanks to gene therapy. It is now 12 months since the Food and Drug Administration rolled out the historic approval of a CRISPR therapy designed for patients suffering from ...

“In the history of heart failure research ... shown improvements in heart function on the order of 5–10%. cBIN1 gene therapy improved function by 30%. “It’s night and day,” Shaw added.

Overall results of the lentiviral gene therapy show promise in overcoming a limitation of AAV-mediated approaches with the ability to bypass anti-AAV antibodies.