Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent after a single infusion of gene therapy, according to the new results of an ...

Ultimately, the ability to realize the full potential of gene therapy to treat rare genetic diseases depends on listening to and addressing patients’ needs. Pfizer aims to establish a new ...

Cancer Gene Therapy is the essential gene and cellular therapy resource for cancer researchers and clinicians, keeping readers up to date with the latest developments in gene and cellular ...

Gene therapy holds promise for treating some of these conditions, and current research advances may soon shift the therapeutic landscape for eye health. However, many obstacles remain in place ...

And, despite the pandemic, 2020 was a landmark year for the 24-year-old, from County Durham, who became the first person in the UK to receive a revolutionary new gene therapy on the NHS.

Chief Justice of India D Y Chandrachud stressed the importance of making costly gene therapy accessible to all, especially those outside urban centers. Speaking at a Bengaluru conference ...

A UK girl born deaf can now hear unaided, after a groundbreaking gene-therapy treatment ... signals to the nerve (shown in yellow in this diagram) "It's wonderful seeing her respond to sound ...

Gene therapy could help obese kids avoid health problems associated with excess weight, including arthritis, a new, preliminary study in mice suggests. The gene therapy prompts cells to convert ...

By September, at least 30 people worldwide had begun a one-time gene therapy outside trials, according to the two drugmakers whose therapies were approved in America. Both treatments involve a ...

Gene Therapy with Fidanacogene Elaparvovec in Adults with Hemophilia B. New England Journal of Medicine , 2024; 391 (12): 1108 DOI: 10.1056/NEJMoa2302982 Cite This Page : ...

Fidanacogene elaparvovec, an adeno-associated virus (AAV) gene-therapy vector for hemophilia B containing a high-activity human factor IX variant (FIX-R338L/FIX-Padua), was associated with ...

After bluebird bio acknowledged troubles keeping its business operational, the gene therapy biotech is launching a restructuring that will reduce the size of its workforce by about 25%.