Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...

Researchers developed a new gene-editing strategy that dramatically boosts the effectiveness of gene therapies in the liver, a breakthrough that could lead to new treatments for about 700 genetic ...

A new discovery offers hope for Huntington’s disease. This discovery provides hope that a DNA repair process may help slow or ...

ETH researchers have developed a new gene switch that can be activated using a commercially available nitroglycerine patch applied to the skin.

More than 1,000 genes may serve as possible treatment targets for individuals with kidney disease, according to a new study, ...

Alternative splicing (AS), a critical process for gene expression regulation ... can contribute to the development of cardiovascular diseases. In addition, multiple hereditary heart-related ...

About Cure Rare Disease (CRD) Cure Rare Disease (CRD) is a nonprofit biotechnology company focused on developing genetic medicines for rare and ultra-rare diseases. CRD is committed to ...

Late-onset Alzheimer's disease is a debilitating ... we can potentially use it to treat both populations," Ma said. By expanding our understanding of genetic risk factors beyond APOE ε4, this ...