Duchenne, one of the most severe forms of muscular dystrophy, affects about one out of every 3,600 boys. The inherited rare ...

A new study introduces an innovative tool for exploring gene-disease connections: the PWAS Hub. This resource is based on the ...

APOE4 carriers had higher blood-brain barrier permeability, even without cognitive decline or amyloid beta buildup, ...

Research collaboration by the Texas A&M Department of Entomology and the U.S. Department of Agriculture, USDA, creates ...

Huntington’s disease poses a threat to the brain—the core governing system of sensation, intellectual ability, nerve-related ...

Discover various promising treatments in development to address the unmet needs of people with Charcot–Marie–Tooth disease.

Arrowhead Pharmaceuticals has entered a worldwide licensing and partnership agreement with Sarepta Therapeutics to develop ...

Chronic diseases like type 2 diabetes and inflammatory disorders have a huge impact on humanity. They are a leading cause of ...

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...

Being at higher risk of heart disease may cause dementia to appear in men a decade before it will occur in similarly at-risk ...

Analyst Joseph Pantginis from H.C. Wainwright maintained a Buy rating on Tenaya Therapeutics (TNYA – Research Report) and keeping the price ...