“There are more than 100,000 adults with DM1 in the US and Europe, making it the most common adult-onset muscular dystrophy. We believe that the market opportunity for a new DM1 therapy is very ...
Ryan Getzlaf and Hawken Miller help to inspire each other every day, and Miller’s battle with Duchenne muscular dystrophy has given Getzlaf a cause to champion away from the rink. Take a look at ...
At the Breakthroughs in Muscular Dystrophy special meeting held in Chicago Nov. 19-20, 2024, and organized by the American Society of Gene & Cell Therapy (ASGCT), multiple interventions at the RNA ...
have been diagnosed with Duchenne Muscular Dystrophy, a rare progressive muscle loss disease. On Saturday at Cherry Rock Park, the group held a Zippy Mile to raise funds to help fight the disease ...
Spain’s ARTHEx Biotech has developed a dual-mechanism approach to treating the most common adult-onset muscular dystrophy, myotonic dystrophy type 1, setting it apart in a burgeoning blockbuster ...
Regenxbio reported Monday the first clinical evidence showing improved muscle function in boys with Duchenne muscular dystrophy following treatment with its experimental gene therapy. The positive ...