The biomedical research community should act quickly and decisively to divorce the two before pushing ahead with well-conceived postnatal and fetal somatic gene therapy protocols. That gene ...
A pioneering therapy aimed at reversing a leading cause of stillbirth and premature birth has shown promising results in animal studies, led by decades of research on the placenta Study: Placental ...
might require prenatal or fetal gene therapy to minimize morbidity. Gene therapy is also being considered for the treatment of inflammatory and infectious diseases of the lung. In these cases ...
A gene therapy based on an enhanced lipid nanoparticle (LNP) loaded with vascular endothelial growth factor (VEGF) mRNA could be developed for the treatment of preeclampsia, according to a study in ...
(Unlike "adult" hemoglobin, fetal hemoglobin doesn't cause sickling.) But a new trial called BEACON, led at Boston Children's ...
The new gene therapies for sickle cell disease—including the gene-editing treatment Casgevy, based on research at Boston ...
Researchers have successfully prevented the development of a fatal neurodegenerative disorder, Gaucher disease, using fetal gene therapy, in mice. The study highlights the potential of using this ...
We recently compiled a list of the 10 Best Gene Therapy Stocks to Buy Right Now. In this article, we are going to take a look ...
The trial is testing base editing — the most precise form of gene therapy yet developed — as a way to boost fetal hemoglobin production. In contrast to conventional gene editing strategies ...
The trial is testing base editing—the most precise form of gene therapy yet developed—as a way to boost fetal hemoglobin production. How base editing works. Credit: Boston Children's Hospital ...