Interius’s breakthrough technology allows precise targeting of gene therapies to specific cells via intravenous administration," said Interius President and CEO, Phil Johnson, M.D. "This milestone ...
In April 2024, Prime Medicine received the go-ahead from the FDA to initiate a phase I/2 trial with PE-based PM359, an ex vivo gene therapy to treat CGD (chronic granulomatous disease).
That is why the company is also working on gene therapy and ex vivo gene-edited cell therapy. “If you’re working in gene editing, you can also work in gene therapy, because you already know a ...
Intellia Therapeutics is pioneering in vivo CRISPR gene editing, aiming for groundbreaking therapies, with NTLA-2001 showing promising results in ATTR amyloidosis, potentially achieving ...
In vivo gene editing for increased accessibility to CRISPR-based therapies Existing gene therapies that use non-viral vectors for therapeutic delivery typically require ex vivo editing. A patient’s ...
Gene therapy and gene editing are on the cutting ... CRISPR-based gene-editing technology to develop both in vivo and ex vivo cancer cell therapies. Analyst Graham Parry says Sanofi is an ...