In the world of biopharmaceutical innovation, 2024 will be remembered as CRISPR’s breakout year. In the spring, five patients with sickle cell disease began treatment with Casgevy, the first FDA ...

Outsourcing can provide a more flexible supply of services with better timelines. What makes Horizon different from the other companies offering CRISPR technologies? CRISPR has opened up a lot of ...

CRISPR-Cas9 genome editing exploits the CRISPR-Cas system to modify a genome in a targeted manner. Guided by RNA, the Cas9 endonuclease breaks DNA at a target sequence. Imprecise repair of the ...

CRISPR is a technology that can be used to edit genes and, as such, will likely change the world. The essence of CRISPR is simple: it’s a way of finding a specific bit of DNA inside a cell.

CTX450 targets ALAS1 for acute hepatic porphyrias. While the timeline for a second drug approval may be years away, the potential of CRISPR Therapeutics’ pipeline presents significant long-term ...

With a multidisciplinary team in his laboratory at the University of California, San Diego, he now develops tools through genetic engineering techniques such as CRISPR to solve the world’s insect ...