In order to address the underlying biology of the disease, we discovered multiple CFTR modulator therapies with distinct and novel mechanisms of action. We have brought forward four medicines that ...
Join Peter Grootenhuis of Vertex Pharmaceuticals as he delivers a brief overview of the drug discovery approaches and challenges to identify small molecules CFTR modulators. These compounds improve ...
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The long breath: Medical advancements giving cystic fibrosis patients a fuller lifeKnowing this, in the early 2000s, researchers began to look for treatment options that addressed the root cause of CF, ...
Other rare mutations that are not eligible for CFTR modulators will be explored as the editing technology matures. “Gene editing is a promising, complex technology, which will take many years to ...
Other rare mutations that are not eligible for CFTR modulators will be explored as the editing technology matures. "Gene editing is a promising, complex technology, which will take many years to ...
The firm's chief scientific officer called the achievement "a major milestone for Spirovant and for the cystic fibrosis ...
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