Knowing this, in the early 2000s, researchers began to look for treatment options that addressed the root cause of CF, ...
ReCode is set to secure up to $15m in funding from the Cystic Fibrosis Foundation to enhance its gene correction research ...
The firm's chief scientific officer called the achievement "a major milestone for Spirovant and for the cystic fibrosis ...
Join Peter Grootenhuis of Vertex Pharmaceuticals as he delivers a brief overview of the drug discovery approaches and challenges to identify small molecules CFTR modulators. These compounds improve ...
in addition to maintenance of wild-type Sprague Dawley strain for additional use Generation and procurement of novel relevant CF animal models to understand newly developed CFTR modulators, and to ...
Other rare mutations that are not eligible for CFTR modulators will be explored as the editing technology matures. “Gene editing is a promising, complex technology, which will take many years to ...
It’s important to take them on an empty stomach. CFTR modulators are a relatively newer class of medications that may change CFTR function and reduce inflammation. However, the overall effect is ...
People with cystic fibrosis have better treatment options available today than ever before, with the advent of ‘CFTR modulator’ drugs. However, there are still many patients who are unable to ...