Colin Farrell rarely opens up about his private life, but in recent times he's made an exception to honour his beloved son ...

Fred Cheng recently celebrated turning 41 by revealing that his focus this year has been on son Asher. On 11 November, the ...

The now-21-year-old has Angelman syndrome, and the actor called his child’s diagnosis “fuel” in choosing to abstain from drugs and alcohol. “James was 2 when I got sober,” the “Total ...

I want the world to treat him with kindness and respect,” the actor says, which has been the driving factor for raising ...

At first he was misdiagnosed as having cerebral palsy, which is common because cerebral palsy and Angelman syndrome share similar characteristics. But by the time he was two he was already having ...

And the 48-year-old actor says all the money in the world hasn't been enough to find somewhere for his son to live that gives him full confidence that all his support and needs wi ...

Colin Farrell is doing his bit to help families with adult children with disabilities like his own son to get the support ...

Ionis has committed to a phase 3 programme for its antisense therapy for rare genetic disorder Angelman syndrome, just weeks after Biogen decided against exercising an option to license the drug.

(RARE) announced Phase 1/2 data in support of the Phase 3 Aspire study for GTX-102, its investigational antisense oligonucleotide for Angelman syndrome. The Phase 1/2 data showed improvements ...

New preclinical data for candidate ETX201 illustrate its potential as a first-in-class gene therapy for Angelman syndrome. Studies in non-human primates demonstrate safety, biodistribution ...

Ultragenyx Pharmaceutical (NASDAQ:RARE) announced Saturday that GTX-102, its candidate for the rare neuro-genetic disorder Angelman syndrome, improved patient outcomes across multiple domains in a ...