Somatic gene transfer with vectors such as adeno-associated virus (AAV) can overcome these limitations. ReGenX's AAV Vector Technology gives extremely efficient and stable gene expression in ...

In a recently released study, researchers at the National Institute of Standards and Technology, the National Institute for ...

A new study published in the peer-reviewed journal Human Gene Therapy involved the generation of a human monoclonal antibody ...

DOI: 10.1056/NEJMoa2410597 Johnny Mahlangu, Could Lentivirus Overcome the AAV Gene-Therapy Challenges in Hemophilia A?, New England Journal of Medicine (2024). DOI: 10.1056/NEJMe2414214 ...

The work by Associate Professor Leszek Lisowski and his Translational Vectorology Research Unit is published in the journal Molecular ... on their inherent safety, AAV vectors, which are most ...